Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia

• 作者Grossman, Mariann; Raper, Steven E.; Kozarsky, Karen; Stein, Evan A.; Engelhardt, John F.; Muller, David; Lupien, Paul J.; Wilson, James M.
• 卷第6卷
• 期第4期
• 印刷ISSN1061-4036
• 电子ISSN1546-1718
• 文件大小1006.38KB
• 发表时间1994
• DOI10.1038/ng0494-335
• 页码335-341