![Efficacy and ototoxicity of different cyclodextrins in Niemann-Pick C disease]()
Efficacy and ototoxicity of different cyclodextrins in Niemann-Pick C diseaseDavidson, Cristin D.; Fishman, Yonatan I.; Puskás, István; Szemán, Julianna; Sohajda, Tamás; McCauliff, Leslie A.; Sikora, Jakub; Storch, Judith; Vanier, Marie T.; Szente, Lajos; Walkley, Steven U.; Dobrenis, Kostantin · Annals of Clinical and Translational Neurology · 2016