1124. Correction of Glycogen Storage Disease Type II by an AAV Vector Encoding Highly-Secreted, Chimeric Acid α-glucosidase
SUN, B; BROWN, T; BIRD, A; SCHNEIDER, A; YOUNG, S; MCVIEWYLIE, A; CHEN, Y; KOEBERL, D
- 期刊名称Molecular Therapy
- 作者SUN, B; BROWN, T; BIRD, A; SCHNEIDER, A; YOUNG, S; MCVIEWYLIE, A; CHEN, Y; KOEBERL, D
- 卷第11卷
- 印刷ISSN1525-0016
- 文件大小87.24KB
- 发表时间2005-08-15
- DOI10.1016/j.ymthe.2005.07.672
- 页码433-433