PTC124 induces CFTR full-length production and activity in children with nonsense-mutation-mediated CF
I. Sermet-Gaudelus; T. Leal; K. De Boeck; G. Casimir; L. Hanssens; P. Hage; D. Roussel; A. Mogenet; S. Hirawat; G.L. Elfring; S. Constantine; L.L. Miller
作者I. Sermet-Gaudelus; T. Leal; K. De Boeck; G. Casimir; L. Hanssens; P. Hage; D. Roussel; A. Mogenet; S. Hirawat; G.L. Elfring; S. Constantine; L.L. Miller