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Long term effects of enzyme replacement therapy in an Italian cohort of type 3 Gaucher patients

Long term effects of enzyme replacement therapy in an Italian cohort of type 3 Gaucher patients

Sechi, Annalisa; Deroma, Laura; Dardis, Andrea; Ciana, Giovanni; Bertin, Nicole; Concolino, Daniela; Linari, Silvia; Perria, Chiara; Bembi, Bruno
  • 期刊名称Molecular Genetics and Metabolism
  • 作者Sechi, Annalisa; Deroma, Laura; Dardis, Andrea; Ciana, Giovanni; Bertin, Nicole; Concolino, Daniela; Linari, Silvia; Perria, Chiara; Bembi, Bruno
  • 卷第113卷
  • 期第3期
  • 印刷ISSN1096-7192
  • 文件大小529.67KB
  • 发表时间2014-11
  • DOI10.1016/j.ymgme.2014.07.022
  • 页码213-218
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