Long term effects of enzyme replacement therapy in an Italian cohort of type 3 Gaucher patients
Sechi, Annalisa; Deroma, Laura; Dardis, Andrea; Ciana, Giovanni; Bertin, Nicole; Concolino, Daniela; Linari, Silvia; Perria, Chiara; Bembi, Bruno
- 期刊名称Molecular Genetics and Metabolism
- 作者Sechi, Annalisa; Deroma, Laura; Dardis, Andrea; Ciana, Giovanni; Bertin, Nicole; Concolino, Daniela; Linari, Silvia; Perria, Chiara; Bembi, Bruno
- 卷第113卷
- 期第3期
- 印刷ISSN1096-7192
- 文件大小529.67KB
- 发表时间2014-11
- DOI10.1016/j.ymgme.2014.07.022
- 页码213-218