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Widespread correction of central nervous system disease after intracranial gene therapy in a feline model of Sandhoff disease

Widespread correction of central nervous system disease after intracranial gene therapy in a feline model of Sandhoff disease

McCurdy, V J; Rockwell, H E; Arthur, J R; Bradbury, A M; Johnson, A K; Randle, A N; Brunson, B L; Hwang, M; Gray-Edwards, H L; Morrison, N E; Johnson, J A; Baker, H J; Cox, N R; Seyfried, T N; Sena-Esteves, M; Martin, D R
  • 期刊名称Gene Therapy
  • 作者McCurdy, V J; Rockwell, H E; Arthur, J R; Bradbury, A M; Johnson, A K; Randle, A N; Brunson, B L; Hwang, M; Gray-Edwards, H L; Morrison, N E; Johnson, J A; Baker, H J; Cox, N R; Seyfried, T N; Sena-Esteves, M; Martin, D R
  • 卷第22卷
  • 期第2期
  • 印刷ISSN0969-7128
  • 电子ISSN1476-5462
  • 文件大小1494.10KB
  • 发表时间2015-2
  • DOI10.1038/gt.2014.108
  • 页码181-189
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