![Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency]()
Gene Therapy for Immunodeficiency Due to Adenosine Deaminase DeficiencyAiuti, Alessandro; Cattaneo, Federica; Galimberti, Stefania; Benninghoff, Ulrike; Cassani, Barbara; Callegaro, Luciano; Scaramuzza, Samantha; Andolfi, Grazia; Mirolo, Massimiliano; Brigida, Immacolata; Tabucchi, Antonella; Carlucci, Filippo; Eibl, Martha; Aker, Memet; Slavin, Shimon; Al-Mousa, Hamoud; Al Ghonaium, Abdulaziz; Ferster, Alina; Duppenthaler, Andrea; Notarangelo, Luigi; Wintergerst, Uwe; Buckley, Rebecca H.; Bregni, Marco; Marktel, Sarah; Valsecchi, Maria Grazia; Rossi, Paolo; Ciceri, Fabio; Miniero, Roberto; Bordignon, Claudio; Roncarolo, Maria-Grazia · New England Journal of Medicine · 2009