Gene therapy using a miniCEP290 fragment delays photoreceptor degeneration in a mouse model of Leber congenital amaurosis (LCA)
Zhang, Wei; Li, Linjing; Su, Qin; Gao, Guangping; Khanna, Hemant
- 期刊名称Human Gene Therapy
- 作者Zhang, Wei; Li, Linjing; Su, Qin; Gao, Guangping; Khanna, Hemant
- 印刷ISSN1043-0342
- 电子ISSN1557-7422
- 文件大小1897.47KB
- 发表时间2017-07-05
- DOI10.1089/hum.2017.049