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[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Therapeutics: Alpha-1 Antitrypsin Augmentation TherapyBorel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Alpha-1 Antitrypsin Transcytosis and SecretionBorel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Pathophysiology of Alpha-1 Antitrypsin Lung DiseaseBorel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Immunohistochemistry Staining for Human Alpha-1 AntitrypsinBorel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Pathophysiology of Alpha-1 Antitrypsin Deficiency Liver DiseaseBorel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Therapeutics: Gene Therapy for Alpha-1 Antitrypsin DeficiencyBorel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Therapeutic Options in Alpha-1 Antitrypsin Deficiency: Liver TransplantationBorel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Genotyping Protocol for the Alpha-1 Antitrypsin (PiZ) Mouse ModelBorel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 ||Borel, Florie; Mueller, Christian · 2017
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Laboratory Diagnosis by GenotypingBorel, Florie; Mueller, Christian · 2017
Recombinant AAV as a Platform for Translating the Therapeutic Potential of RNA InterferenceBorel, Florie; Kay, Mark A; Mueller, Christian · Molecular Therapy · 2014
Safe and effective superoxide dismutase 1 silencing using artificial microRNA in macaquesBorel, Florie; Gernoux, Gwladys; Sun, Huaming; Stock, Rachel; Blackwood, Meghan; Brown, Robert H.; Mueller, Christian · Science Translational Medicine · 2018
90. Vector Biodistribution After Recombinant AAVrh10 Intrathecal Delivery in Non-Human PrimatesGernoux, Gwladys; Borel, Florie; Gao, Guangping; Brown, Robert H.; Mueller, Christian · Molecular Therapy · 2016
[Methods in Molecular Biology] Alpha-1 Antitrypsin Deficiency Volume 1639 || Measuring and Interpreting Serum AAT ConcentrationBorel, Florie; Mueller, Christian · 2017