Cardiac features and effects of enzyme replacement therapy in Taiwanese patients with Mucopolysaccharidosis IVA
Lin, Hsiang-Yu; Chen, Ming-Ren; Lin, Shan-Miao; Hung, Chung-Lieh; Niu, Dau-Ming; Chuang, Chih-Kuang; Lin, Shuan-Pei
- 期刊名称Orphanet Journal of Rare Diseases
- 作者Lin, Hsiang-Yu; Chen, Ming-Ren; Lin, Shan-Miao; Hung, Chung-Lieh; Niu, Dau-Ming; Chuang, Chih-Kuang; Lin, Shuan-Pei
- 卷第13卷
- 期第1期
- 电子ISSN1750-1172
- 文件大小1550.97KB
- 发表时间2018-12
- DOI10.1186/s13023-018-0883-6