Identification of Novel Antisense-Mediated Exon Skipping Targets in DYSF for Therapeutic Treatment of Dysferlinopathy
Lee, Joshua J.A.; Maruyama, Rika; Duddy, William; Sakurai, Hidetoshi; Yokota, Toshifumi
- 期刊名称Molecular Therapy - Nucleic Acids
- 作者Lee, Joshua J.A.; Maruyama, Rika; Duddy, William; Sakurai, Hidetoshi; Yokota, Toshifumi
- 卷第13卷
- 印刷ISSN2162-2531
- 文件大小1316.01KB
- 发表时间2018-12
- DOI10.1016/j.omtn.2018.10.004
- 页码596-604