A consensus conference for cognitive endpoints for clinical trials and natural history studies in MPS diseases
Shapiro, Elsa G.; Greenberg, Jennifer L.; Dant, Mark; Lavery, Christine; van der Lee, Johanna; Janzen, Darren; Delaney, Kathleen; Bigger, Brian
- 期刊名称Molecular Genetics and Metabolism
- 作者Shapiro, Elsa G.; Greenberg, Jennifer L.; Dant, Mark; Lavery, Christine; van der Lee, Johanna; Janzen, Darren; Delaney, Kathleen; Bigger, Brian
- 卷第123卷
- 期第2期
- 印刷ISSN1096-7192
- 文件大小52.10KB
- 发表时间2018-02
- DOI10.1016/j.ymgme.2017.12.354