Highly efficient therapeutic gene editing of human hematopoietic stem cells

• 期刊名称Nature Medicine
• 作者Wu, Yuxuan; Zeng, Jing; Roscoe, Benjamin P.; Liu, Pengpeng; Yao, Qiuming; Lazzarotto, Cicera R.; Clement, Kendell; Cole, Mitchel A.; Luk, Kevin; Baricordi, Cristina; Shen, Anne H.; Ren, Chunyan; Esrick, Erica B.; Manis, John P.; Dorfman, David M.; Williams, David A.; Biffi, Alessandra; Brugnara, Carlo; Biasco, Luca; Brendel, Christian; Pinello, Luca; Tsai, Shengdar Q.; Wolfe, Scot A.; Bauer, Daniel E.
• 印刷ISSN1078-8956
• 电子ISSN1546-170X
• 文件大小8624.53KB
• 发表时间2019-3-25
• DOI10.1038/s41591-019-0401-y