Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A
Lostal, William; Roudaut, Carinne; Faivre, Marine; Charton, Karine; Suel, Laurence; Bourg, Nathalie; Best, Heather; Smith, John Edward; Gohlke, Jochen; Corre, Guillaume; Li, Xidan; Elbek, Zaher; Knoell, Ralph; Deschamps, Jack-Yves; Granzier, Henk; Richard, Isabelle
- 期刊名称Science Translational Medicine
- 作者Lostal, William; Roudaut, Carinne; Faivre, Marine; Charton, Karine; Suel, Laurence; Bourg, Nathalie; Best, Heather; Smith, John Edward; Gohlke, Jochen; Corre, Guillaume; Li, Xidan; Elbek, Zaher; Knoell, Ralph; Deschamps, Jack-Yves; Granzier, Henk; Richard, Isabelle
- 卷第11卷
- 期第520期
- 印刷ISSN1946-6234
- 电子ISSN1946-6242
- 文件大小7810.77KB
- 发表时间2019-11-27
- DOI10.1126/scitranslmed.aat6072