European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene
Haas, Manuel; Vlcek, Viktor; Balabanov, Pavel; Salmonson, Tomas; Bakchine, Serge; Markey, Greg; Weise, Martina; Schlosser-Weber, Gabriele; Brohmann, Henning; Yerro, Concepcion Prieto; Mendizabal, Macarena Rodriguez; Stoyanova-Beninska, Violeta; Hillege, Hans L.
- 期刊名称Neuromuscular Disorders
- 作者Haas, Manuel; Vlcek, Viktor; Balabanov, Pavel; Salmonson, Tomas; Bakchine, Serge; Markey, Greg; Weise, Martina; Schlosser-Weber, Gabriele; Brohmann, Henning; Yerro, Concepcion Prieto; Mendizabal, Macarena Rodriguez; Stoyanova-Beninska, Violeta; Hillege, Hans L.
- 卷第25卷
- 期第1期
- 印刷ISSN0960-8966
- 文件大小985.38KB
- 发表时间2015-01
- DOI10.1016/j.nmd.2014.11.011
- 页码5-13